This phase I/II trial studies the side effects and best dose of universal donor natural killer cells (UD-NK) when given together with fludarabine and cytarabine and tests how well it works in treating acute myeloid leukemia (AML) that has come back after a period of improvement (relapsed) or that does not respond to treatment (refractory). Natural killer (NK) cells are cells that are a part of the immune system. NK cells have been shown to kill different types of cancer. However, these cells are only present in the body in small numbers. UD-NK cells come from donors unrelated to the patient. UD-NK cells are grown into large numbers in a laboratory and stored until a patient needs them. Upon administration, the UD-NK cells target and destroy cancer cells. Before UD-NK cells are given to the patient, chemotherapy is given. Chemotherapy drugs, such as fludarabine and cytarabine, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Giving UD-NK cells after fludarabine and cytarabine may work better in treating relapsed or refractory AML.
Additional locations may be listed on ClinicalTrials.gov for NCT05503134.
Locations matching your search criteria
United States
Ohio
Columbus
Nationwide Children's HospitalStatus: Active
Contact: Margaret Lamb
Phone: 614-722-3550
PRIMARY OBJECTIVES:
I. To determine the safety and recommended phase II dose of adoptive NK cell therapy using membrane-bound interleukin-21-expanded haploidentical natural killer cells (UD-NK cells) in pediatric and young adult patients with relapsed/refractory AML. (Dose finding phase)
II. To estimate the complete response rate of UD-NK cells with fludarabine/cytarabine (FLA) chemotherapy in pediatric and young adult patients with relapsed/refractory AML. (Expansion phase)
SECONDARY OBJECTIVE:
I. To estimate the efficacy of UD-NK cells with FLA chemotherapy in pediatric and young adult patients with relapsed/refractory AML.
EXPLORATORY OBJECTIVES:
I. To determine the immunophenotype and function of UD-NK cells.
II. To characterize in vivo expansion of UD-NK cells.
III. To determine the persistence of UD-NK cells.
OUTLINE: This is a phase I, dose-escalation study of UD-NK cells followed by a phase II study.
Patients receive fludarabine intravenously (IV) over 30 minutes and cytarabine IV over 4 hours on days 1-5. Patients also receive UD-NK cells IV three times a week (TIW) for two weeks from days 8-36. Patients with less than complete response (CR) or with persistent minimal residual disease (MRD) positivity after cycle 1 or who require an additional cycle for bridging to hematopoietic stem cell transplant (HSCT) may receive 1 additional cycle of fludarabine, cytarabine and UD-NK cells as above. Patients also undergo echocardiography (ECHO) during screening and collection of blood samples as well as bone marrow aspiration and biopsy throughout the study. Patients may also undergo lumbar puncture throughout the study.
After completion of study treatment, patients are followed up at day 56 and then for 12 months after the first UD-NK cell infusion.
Lead OrganizationNationwide Children's Hospital
Principal InvestigatorMargaret Lamb