Blinatumomab and Asciminib for the Treatment of Patients with Philadelphia Chromosome-Positive Acute Lymphoblastic Leukemia
This phase I/II trial tests how well blinatumomab and asciminib work in treating patients with Philadelphia chromosome-positive acute lymphoblastic leukemia (ALL). [Blinatumomab is a monoclonal antibody that may interfere with the ability of cancer cells to grow and spread. Asciminib is in a class of medications called tyrosine kinase inhibitors. It works by blocking the action of an abnormal protein that signals cancer cells to multiply, which may help keep cancer cells from growing. Giving blinatumomab and asciminib in combination may work to treat patients with Philadelphia chromosome positive ALL.
Inclusion Criteria
- Diagnosis of one of the following: * Patients ≥ 18 years of age with previously untreated or minimally pretreated Ph-positive ALL who are not suitable candidates for intensive chemotherapy. Patients who have received no more than one or two courses of chemotherapy with or without other tyrosine kinase inhibitors (TKIs) are considered minimally pretreated and still eligible if they have persistently detectable MRD. ** If they are in morphologic remission at enrollment, they are evaluable only MRD responses, relapse-free survival (RFS) and overall survival (OS) * Patients ≥ 12 years of age with relapsed/refractory Ph-positive ALL or with previously treated lymphoid blast phase chronic myeloid leukemia (CML)
- Performance status ≤ 2 (Eastern Cooperative Oncology Group [ECOG] Scale) if age ≥ 18 years or Lansky ≥ 50 if age < 18 years
- Weight ≥ 40kg
- Total serum bilirubin =< 2 x upper limit of normal (ULN), unless due to Gilbert’s syndrome (unless the increased values are judged to be leukemia disease related)
- Alanine aminotransferase (ALT) =< 3 x ULN, OR aspartate aminotransferase (AST) =< 3 x ULN (unless the increased values are judged to be leukemia disease related)
- Creatinine clearance ≥ 30 mL/min
- Serum lipase and amylase < 1.5 x ULN
- Adequate cardiac function as assessed clinically by history and physical examination
- For females of childbearing potential, a negative urine pregnancy test must be documented
- Willingness to use adequate contraception prior to study entry, for the duration of study participation, and for 4 months after completion of study participation. For women of child-bearing potential, adequate methods of contraception include: complete abstinence, hormonal contraception (i.e. birth control pills, injection, implant, transdermal patch, vaginal ring), intrauterine device (IUD), tubal ligation or hysterectomy, subject/partner post vasectomy, implantable or injectable contraceptives, and condoms plus spermicide
- Ability to understand and the willingness to sign a written informed consent document
- Signed informed consent
Exclusion Criteria
- Active serious infection not controlled by oral or intravenous antibiotics
- Active secondary malignancy other than skin cancer (e.g., basal cell carcinoma or squamous cell carcinoma) that in the investigator’s opinion will shorten survival to less than 1 year
- Active grade III-V cardiac failure as defined by the New York Heart Association Criteria
- Prolonged QTc interval on pre-entry electrocardiogram (> 470 msec) unless corrected after electrolyte replacement or approved by cardiologist
- History or presence of clinically relevant central nervous system (CNS) pathology such as epilepsy, childhood or adult seizure, paresis, aphasia, stroke, severe brain injuries, dementia, Parkinson’s disease, cerebellar disease, organic brain syndrome, or psychosis. (Patients with active CNS leukemia will NOT be excluded)
- Treatment with any investigational antileukemic agents or chemotherapy agents in the last 7 days before study entry, unless full recovery from side effects has occurred or patient has rapidly progressive disease judged to be life-threatening by the investigator
- Pregnant and lactating women will not be eligible; women of childbearing potential should have a negative pregnancy test prior to entering on the study and be willing to practice methods of contraception. Women do not have childbearing potential if they have had a hysterectomy or are postmenopausal without menses for 12 months. In addition, men enrolled on this study should understand the risks to any sexual partner of childbearing potential and should practice an effective method of birth control
Additional locations may be listed on ClinicalTrials.gov for NCT06308588.
Locations matching your search criteria
United States
Texas
Houston
PRIMARY OBJECTIVES:
I. To determine the minimum safe and biologically effective dose of asciminib in combination with blinatumomab. (Phase I)
II. To evaluate the rate of next-generation sequencing (NGS) measurable residual disease (MRD) negativity using the clonoSEQ® assay in cohort 1 (newly diagnosed Philadelphia [Ph]-positive acute lymphoblastic leukemia [ALL]) and the overall response (complete remission [CR]+complete remission with incomplete hematologic recovery [CRi]) rate in cohort 2 (relapsed/refractory disease). (Phase II)
SECONDARY OBJECTIVES:
I. To evaluate other clinical efficacy endpoints (complete molecular response [CMR] rate, CR rate, relapse-free survival and overall survival).
II. To determine the safety of the combination regimen.
EXPLORATORY OBJECTIVES:
I. To characterize the role of ABL1 kinase domain mutations on treatment failure and relapse.
II. To assess concordance/discordance between MRD assessed by polymerase chain reaction (PCR) for BCR::ABL1 and next-generation sequencing MRD.
III. To determine the effect of the combination regimen on immune cell subsets.
OUTLINE: This is a phase I, dose-escalation study of asciminib in combination with blinatumomab followed by a phase II study.
COMBINATION: Patients receive asciminib orally (PO) twice daily (BID) in cycles 1-5. Patients also receive blinatumomab intravenously (IV) continuously on days 4-31 of cycle 1, and days 1-28 of cycles 2-5. Cycle 1 will last 45 days. Subsequent treatment repeats every 42 days for up to 4 additional cycles (5 cycles total) in the absence of disease progression or unacceptable toxicity.
MAINTENANCE: Patients continue to receive asciminib PO BID for at least 5 years in the absence of disease progression or unacceptable toxicity. Patients with loss of molecular response may receive blinatumomab IV over 4 weeks. Treatment with blinatumomab may repeat every 6 weeks for up to 4 cycles in the absence of disease progression of unacceptable toxicity.
Patients also undergo echocardiography or multigated acquisition scan (MUGA) during screening and undergo bone marrow aspiration and blood sample collection at screening and on study.
After completion of study treatment, patients are followed up at 30 days and then every 6 months thereafter.
Trial PhasePhase I/II
Trial Typetreatment
Lead OrganizationM D Anderson Cancer Center
Principal InvestigatorNicholas Short
- Primary ID2024-0054
- Secondary IDsNCI-2024-02121
- ClinicalTrials.gov IDNCT06308588